Imagine knowing in your 20s or 30s that you carry a gene that will cause your mind and body to slowly unravel.

Huntington's disease is inherited, relentless, and fatal, and there is no cure. Families live with the certainty of decline stretching across generations.

Now, a new treatment is being widely reported as a breakthrough.

Last week, gene therapy company uniQure announced that a one-time brain infusion appeared to slow the disease in a small clinical study .

If confirmed, this would not only be a landmark for Huntington's disease but potentially the first time a gene therapy has shown promise in any adult-onset neurodegenerative disorder.

But the results, which were announced in a press release, are early, unreviewed, and based on external comparisons. So, while these findin

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